SN38

SN38

SN38 製品リスト

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治験薬に関する情報

英語名研究コード研究開発ステージ会社適応症臨床試験
ALXN-2220ALXN2220; ALXN-2220; NI006; NI-006Phase 3 ClinicalAstraZeneca global R & D (China) Co Ltd
Cardiomyopathies; Transthyretin amyloidosis
詳細
Nexiguran ziclumeranNTLA-2001Phase 3 ClinicalIntellia Therapeutics Inc
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Peripheral Nervous System Diseases; Metabolism, Inborn Errors; Polyneuropathies; Genetic Diseases, Inborn; Metabolic Diseases; Cardiomyopathies; Amyloidosis; Nervous System Diseases; Neuromuscular Diseases; Heredodegenerative Disorders, Nervous System; Neurodegenerative Diseases; Amyloid Neuropathies; Transthyretin amyloidosis
詳細
NNC6019-0001NNC6019-0001; NNC-6019; PRX-004Phase 2 ClinicalNovo Nordisk A/S
Cardiomyopathies; Transthyretin amyloidosis
詳細
NI-006NI-006Phase 1 ClinicalNeurimmune Ag
Cardiomyopathies; Transthyretin amyloidosis
詳細
NucresiranALNTTRsc-04Phase 1 ClinicalAlnylam Pharmaceuticals Inc
Transthyretin amyloidosis
詳細

市販薬剤に関する情報

英語名研究コード研究開発ステージ会社オリジナル製品名最初に承認をした国最初の適応症最初に承認を受けた会社承認された日付適応症臨床試験
PatisiranSAR-438037; GENZ-438027; ALN-TTR02; ALN-18328ApprovedAlnylam Pharmaceuticals IncOnpattroUnited StatesAmyloid Neuropathies, FamilialAlnylam Pharmaceuticals Inc2018-08-10
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Polyneuropathies; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies
詳細
VutrisiranALN-TTRSC02ApprovedAlnylam Pharmaceuticals IncAMVUTTRAUnited StatesAmyloid Neuropathies, Familial; Transthyretin amyloidosisAlnylam Pharmaceuticals Inc2022-06-13
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis
詳細
AcoramidisAG-10; ALXN-2060; ALXN 2060; BBP-265ApprovedStanford UniversityAttrubyUnited StatesTransthyretin amyloidosisBridgebio Pharma Inc2024-11-22
Polyneuropathies; Heart Diseases; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies
詳細
Inotersen sodiumISIS-420915; GSK-2998728ApprovedIonis Pharmaceuticals IncTegsediEUAmyloidosisAkcea Therapeutics Ireland Ltd2018-07-05
Adenomatous Polyposis Coli; Amyloid Neuropathies, Familial; Amyloidosis; Transthyretin amyloidosis
詳細
TafamidisPF-6291826; Fx-1006A; PF-06291826; FX-1006AApprovedPfizer Inc维万心, VYNDAMAXUnited StatesHeart DiseasesFoldrx Pharmaceuticals Inc2019-05-03
Heart Diseases; Transthyretin amyloidosis
詳細
EplontersenIONIS-TTR-LRx; AKCEA-TTR-LRx; ION-682884; ION-TTR-LRxApprovedIonis Pharmaceuticals IncWAINUAUnited StatesTransthyretin amyloidosisAstrazeneca Ab2023-12-21
Amyloid Neuropathies, Familial; Cardiomyopathies; Transthyretin amyloidosis
詳細
Tafamidis MeglumineFX-1006A; PF-6291826; Fx-1006A; PF-06291826ApprovedPfizer Inc维达全, VyndaqelEUAmyloidosisPfizer Europe Ma Eeig2011-11-16
Amyloid Neuropathies, Familial; Immunoglobulin Light-chain Amyloidosis; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies
詳細